Maniatis, T. (2024). From bacterial operons to gene therapy: 50 years of the journal Cell. Cell, 187(23), 6417–6420. https://doi.org/10.1016/j.cell.2024.10.037
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Genetic Therapy
Zuccaro, M. V., LeDuc, C. A., & Thaker, V. V. (2024). Updates on Rare Genetic Variants, Genetic Testing, and Gene Therapy in Individuals With Obesity. Current Obesity Reports, 13(3), 626–641. https://doi.org/10.1007/s13679-024-00567-y
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Li, Y., Yang, R. R., Li, Y. S., Hsu, C. W., Jenny, L. A., Kong, Y., Ruan, M. Z., Sparrow, J. R., & Tsang, S. H. (2024). Evaluating precision medicine approaches for gene therapy in patient-specific cellular models of Bietti crystalline dystrophy. JCI insight, 9(16), e177231. https://doi.org/10.1172/jci.insight.177231
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Abela, L., Gianfrancesco, L., Tagliatti, E., Rossignoli, G., Barwick, K., Zourray, C., Reid, K. M., Budinger, D., Ng, J., Counsell, J., Simpson, A., Pearson, T. S., Edvardson, S., Elpeleg, O., Brodsky, F. M., Lignani, G., Barral, S., & Kurian, M. A. (2024). Neurodevelopmental and synaptic defects in DNAJC6 parkinsonism, amenable to gene therapy. Brain, 147(6), 2023–2037. https://doi.org/10.1093/brain/awae020
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Breazzano, M. P., Batson, S. A., Tsang, S. H., & Chen, R. W. S. (2022). Surgical Approach with Pars Plana Vitrectomy for Subretinal Gene Therapy. Retinitis Pigmentosa, 393–399. https://doi.org/10.1007/978-1-0716-2651-1_35
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Wu, W.-H., Tso, A., Breazzano, M. P., Jenny, L. A., Levi, S. R., Tsang, S. H., & Quinn, P. M. J. (2022). Culture of Human Retinal Explants for Ex Vivo Assessment of AAV Gene Delivery. Retinitis Pigmentosa, 303–311. https://doi.org/10.1007/978-1-0716-2651-1_28
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Pereira, E. M. (2022). Gene Therapy Update. Pediatrics In Review, 43(9), 536–537. https://doi.org/10.1542/pir.2021-005091
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Kajtna, J., Tsang, S. H., & Koch, S. F. (2022). Late-stage rescue of visually guided behavior in the context of a significantly remodeled retinitis pigmentosa mouse model. Cellular and Molecular Life Sciences, 79(3). https://doi.org/10.1007/s00018-022-04161-0
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Kanter, J., Walters, M. C., Krishnamurti, L., Mapara, M. Y., Kwiatkowski, J. L., Rifkin-Zenenberg, S., Aygun, B., Kasow, K. A., Pierciey, F. J., Bonner, M., Miller, A., Zhang, X., Lynch, J., Kim, D., Ribeil, J.-A., Asmal, M., Goyal, S., Thompson, A. A., & Tisdale, J. F. (2022). Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease. New England Journal of Medicine, 386(7), 617–628. https://doi.org/10.1056/nejmoa2117175
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