Peterschmitt, M. J., Saiki, H., Hatano, T., Gasser, T., Isaacson, S. H., Gaemers, S. J. M., Minini, P., Saubadu, S., Sharma, J., Walbillic, S., Alcalay, R. N., Cutter, G., Hattori, N., Höglinger, G. U., Marek, K., Schapira, A. H. V., Scherzer, C. R., Simuni, T., … Fischer, T. Z. (2022). Safety, Pharmacokinetics, and Pharmacodynamics of Oral Venglustat in Patients with Parkinson’s Disease and a GBA Mutation: Results from Part 1 of the Randomized, Double-Blinded, Placebo-Controlled MOVES-PD Trial. Journal of Parkinson’s Disease, 12(2), 557–570. https://doi.org/10.3233/jpd-212714
Subjects:
Pathophysiology of Parkinson's Disease
(OpenAlex Topic)
Lysosomal Storage Disorders in Human Health and Disease
(OpenAlex Topic)
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Glucosylceramidase
(MeSH)
Parkinson Disease
(MeSH)
Publication Type:
Article
Unique ID:
10.3233/JPD-212714
PMID:
DOI:
Journal:
Publication Date:
Data Source:
Web of Science