Polyneuropathies

Subject Vocabulary
MeSH
Unique ID
D011115

Impact of vutrisiran on exploratory cardiac parameters in hereditary transthyretin‐mediated amyloidosis with polyneuropathy

Garcia‐Pavia, P., Grogan, M., Kale, P., Berk, J. L., Maurer, M. S., Conceição, I., Di Carli, M., Solomon, S. D., Chen, C., Yureneva, E., Vest, J., & Gillmore, J. D. (2024). Impact of vutrisiran on exploratory cardiac parameters in hereditary transthyretin‐mediated amyloidosis with polyneuropathy. European Journal of Heart Failure, 26(2), 397–410. Portico. https://doi.org/10.1002/ejhf.3138
Authors:
Pablo García‐Pavía
Martha Grogan
Parag Kale
John L. Berk
Mathew S. Maurer
Isabel Conceição
Marcelo F. Di Carli
Scott D. Solomon
Chongshu Chen
Elena Yureneva
John Vest
Julian D. Gillmore
Affiliated Authors:
Mathew S. Maurer
Author Keywords:
vutrisiran
hereditary transthyretin-mediated amyloidosis
cardiomyopathy
nt-probnp
echocardiography
tc-99m scintigraphy
<sup>99m</sup>tc scintigraphy
99mtc scintigraphy
hereditary transthyretin‐mediated amyloidosis
nt‐probnp
Publication Type:
Article
Unique ID:
10.1002/ejhf.3138
PMID:
Publication Date:
Data Source:
OpenAlex

Record Created:

Diagnosis and treatment of hereditary transthyretin amyloidosis with polyneuropathy in the United States: Recommendations from a panel of experts

Karam, C., Mauermann, M. L., Gonzalez‐Duarte, A., Kaku, M. C., Ajroud‐Driss, S., Brannagan, T. H., & Polydefkis, M. (2024). Diagnosis and treatment of hereditary transthyretin amyloidosis with polyneuropathy in the United States: Recommendations from a panel of experts. Muscle & Nerve, 69(3), 273–287. Portico. https://doi.org/10.1002/mus.28026
Authors:
Chafic Karam
Michelle L Mauermann
Alejandra Gonzalez-Duarte
Michelle C Kaku
Senda Ajroud-Driss
Thomas H Brannagan
Michael Polydefkis
Affiliated Authors:
Thomas H Brannagan
Author Keywords:
attrv amyloid neuropathy
attrv amyloidosis with polyneuropathy
diagnosis guidelines
hereditary transthyretin-mediated (hattr) amyloidosis
treatment recommendations
Publication Type:
Article
Unique ID:
10.1002/mus.28026
PMID:
Journal:
Publication Date:
Data Source:
PubMed

Record Created:

Heterogeneous worldwide access and pricing of Tafamidis

Wardhere, A., Bampatsias, D., Fine, N., Garcia-Pavia, P., Grogan, M., Kristen, A. V., Damy, T., Sekijima, Y., & Maurer, M. S. (2023). Heterogeneous worldwide access and pricing of Tafamidis. Amyloid, 31(1), 73–75. https://doi.org/10.1080/13506129.2023.2263620
Authors:
Abdirahman Wardhere
Dimitrios Bampatsias
Nowell Fine
Pablo Garcia-Pavia
Martha Grogan
Arnt V Kristen
Thibaud Damy
Yoshiki Sekijima
Mathew S Maurer
Affiliated Authors:
Abdirahman Wardhere
Dimitrios Bampatsias
Mathew S Maurer
Publication Type:
Article
Unique ID:
10.1080/13506129.2023.2263620
PMID:
Journal:
Publication Date:
Data Source:
PubMed

Record Created:

Updated consensus statement: Intravenous immunoglobulin in the treatment of neuromuscular disorders report of the AANEM ad hoc committee

Tavee, J., Brannagan, T. H., Lenihan, M. W., Muppidi, S., Kellermeyer, L., & D Donofrio, P. (2023). Updated consensus statement: Intravenous immunoglobulin in the treatment of neuromuscular disorders report of the AANEM ad hoc committee. Muscle & Nerve, 68(4), 356–374. Portico. https://doi.org/10.1002/mus.27922
Authors:
Jinny Tavee
Thomas H Brannagan
Michael W Lenihan
Sri Muppidi
Liz Kellermeyer
Peter D Donofrio
Affiliated Authors:
Thomas H Brannagan
Author Keywords:
gammaglobulin
ivig
myasthenia gravis
myositis
neuropathy
Publication Type:
Article
Unique ID:
10.1002/mus.27922
PMID:
Journal:
Publication Date:
Data Source:
PubMed

Record Created: