CRISPR-AsCas12a Efficiently Corrects a GPR143 Intronic Mutation in Induced Pluripotent Stem Cells from an Ocular Albinism Patient

Torriano, S., Baulier, E., Garcia Diaz, A., Corneo, B., & Farber, D. B. (2022). CRISPR-AsCas12a Efficiently Corrects a GPR143 Intronic Mutation in Induced Pluripotent Stem Cells from an Ocular Albinism Patient. The CRISPR Journal, 5(3), 457–471. https://doi.org/10.1089/crispr.2021.0110
Authors:
Simona Torriano
Edouard Baulier
Alejandro Garcia Diaz
Barbara Corneo
Debora B Farber
Affiliated Authors:
Alejandro Garcia Diaz
Barbara Corneo
Publication Type:
Article
Unique ID:
10.1089/crispr.2021.0110
PMID:
Publication Date:
Data Source:
PubMed

Record Created: