Safety and efficacy of venglustat in GBA1-associated Parkinson's disease: an international, multicentre, double-blind, randomised, placebo-controlled, phase 2 trial

Giladi, N., Alcalay, R. N., Cutter, G., Gasser, T., Gurevich, T., Höglinger, G. U., Marek, K., Pacchetti, C., Schapira, A. H. V., Scherzer, C. R., Simuni, T., Minini, P., Sardi, S. P., & Peterschmitt, M. J. (2023). Safety and efficacy of venglustat in GBA1-associated Parkinson’s disease: an international, multicentre, double-blind, randomised, placebo-controlled, phase 2 trial. The Lancet Neurology, 22(8), 661–671. https://doi.org/10.1016/s1474-4422(23)00205-3
Authors:
Nir Giladi
Roy N Alcalay
Gary Cutter
Thomas Gasser
Tanya Gurevich
Günter U Höglinger
Kenneth Marek
Claudio Pacchetti
Anthony H V Schapira
Clemens R Scherzer
Tanya Simuni
Pascal Minini
S Pablo Sardi
M Judith Peterschmitt
Affiliated Authors:
Roy N Alcalay
Subjects:
Publication Type:
Article
Unique ID:
10.1016/s1474-4422(23)00205-3
PMID:
Journal:
Publication Date:
Data Source:
PubMed

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