Ziegler, A., Carroll, J., Bain, J. M., Sands, T. T., Fee, R. J., Uher, D., Kanner, C. H., Montes, J., Glass, S., Douville, J., Mignon, L., Gleeson, J. G., Crooke, S. T., & Chung, W. K. (2024). Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder. Nature Medicine. https://doi.org/10.1038/s41591-024-03197-y
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Article
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10.1038/s41591-024-03197-y
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PubMed
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