Wu, W.-H., Tsai, Y.-T., Huang, I.-W., Cheng, C.-H., Hsu, C.-W., Cui, X., Ryu, J., Quinn, P. M. J., Caruso, S. M., Lin, C.-S., & Tsang, S. H. (2022). CRISPR genome surgery in a novel humanized model for autosomal dominant retinitis pigmentosa. Molecular Therapy, 30(4), 1407–1420. https://doi.org/10.1016/j.ymthe.2022.02.010
Subjects:
Retinal Degeneration
(MeSH)
Retinitis Pigmentosa
(MeSH)
Molecular Mechanisms of Retinal Degeneration and Regeneration
(OpenAlex Topic)
DNA Nanotechnology and Bioanalytical Applications
(OpenAlex Topic)
Publication Type:
Article
Unique ID:
10.1016/j.ymthe.2022.02.010
PMID:
Journal:
Publication Date:
Data Source:
Scopus