Fragile X Syndrome Patient-Derived Neurons Developing in the Mouse Brain Show FMR1-Dependent Phenotypes

Krzisch, M. A., Wu, H., Yuan, B., Whitfield, T. W., Liu, X. S., Fu, D., Garrett-Engele, C. M., Khalil, A. S., Lungjangwa, T., Shih, J., Chang, A. N., Warren, S., Cacace, A., Andrykovich, K. R., Rietjens, R. G. J., Wallace, O., Sur, M., Jain, B., & Jaenisch, R. (2023). Fragile X Syndrome Patient–Derived Neurons Developing in the Mouse Brain Show FMR1-Dependent Phenotypes. Biological Psychiatry, 93(1), 71–81. https://doi.org/10.1016/j.biopsych.2022.08.020
Authors:
Marine A Krzisch
Hao Wu
Bingbing Yuan
Troy W Whitfield
X Shawn Liu
Dongdong Fu
Carrie M Garrett-Engele
Andrew S Khalil
Tenzin Lungjangwa
Jennifer Shih
Aaron N Chang
Stephen Warren
Angela Cacace
Kristin R Andrykovich
Rosalie G J Rietjens
Owen Wallace
Mriganka Sur
Bhav Jain
Rudolf Jaenisch
Affiliated Authors:
X Shawn Liu
Subjects:
Author Keywords:
cgg repeats
crispr/cas9
engraftment
fmrp
fragile x syndrome
phenotype
single-cell sequencing
Publication Type:
Article
Unique ID:
10.1016/j.biopsych.2022.08.020
PMID:
Publication Date:
Data Source:
PubMed

Record Created: