Estimating Meaningful Differences in Measures of Neuropathic Impairment, Health‐Related Quality of Life, and Nutritional Status in Patients With Hereditary Transthyretin Amyloidosis

Folkvaljon, F., Gertz, M., Gillmore, J. D., Khella, S., Masri, A., Maurer, M. S., Cruz, M. W., Wixner, J., Chen, J., Reicher, B., Kwoh, J., Yarlas, A., & Berk, J. L. (2024). Estimating Meaningful Differences in Measures of Neuropathic Impairment, Health‐Related Quality of Life, and Nutritional Status in Patients With Hereditary Transthyretin Amyloidosis. Muscle & Nerve, 71(1), 96–107. Portico. https://doi.org/10.1002/mus.28299
Authors:
Folke Folkvaljon
Morie A. Gertz
Julian D. Gillmore
Sami Khella
Ahmad Masri
Mathew S. Maurer
Márcia Waddington‐Cruz
Jonas Wixner
Jersey Chen
Barry Reicher
Jesse Kwoh
Aaron Yarlas
John L. Berk
Affiliated Authors:
Mathew S. Maurer
Columbia Affiliation:
Subjects:
Amyloid Neuropathies, Familial (MeSH)
Quality of Life (MeSH)
Nutritional Status (MeSH)
Molecular Mechanisms of Amyloidosis (OpenAlex Topic)
Genetic Disorders Causing Tissue Mineralization Abnormalities (OpenAlex Topic)
Mineral Metabolism in Chronic Kidney Disease (OpenAlex Topic)
Author Keywords:
anchor-based estimates
antisense oligonucleotide
eplontersen
hereditary transthyretin amyloidosis with polyneuropathy
meaningful difference
anchor‐based estimates
elink
Publication Type:
Article
Unique ID:
10.1002/mus.28299
PMID:
39552102
DOI:
10.1002/mus.28299
Journal:
Muscle and Nerve
Publication Date:
Data Source:
OpenAlex
Source Link:
View OpenAlex Record
View PubMed Record
View Web of Science Record
View Scopus Record

Record Created: