Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder

Ziegler, A., Carroll, J., Bain, J. M., Sands, T. T., Fee, R. J., Uher, D., Kanner, C. H., Montes, J., Glass, S., Douville, J., Mignon, L., Gleeson, J. G., Crooke, S. T., & Chung, W. K. (2024). Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder. Nature Medicine. https://doi.org/10.1038/s41591-024-03197-y
Authors:
Alban Ziegler
Joanne Carroll
Jennifer M Bain
Tristan T Sands
Robert J Fee
David Uher
Cara H Kanner
Jacqueline Montes
Sarah Glass
Julie Douville
Laurence Mignon
Joseph G Gleeson
Stanley T Crooke
Wendy K Chung
Affiliated Authors:
Alban Ziegler
Joanne Carroll
Jennifer M Bain
Tristan T Sands
Robert J Fee
David Uher
Cara H Kanner
Jacqueline Montes
Wendy K Chung
Publication Type:
Article
Unique ID:
10.1038/s41591-024-03197-y
PMID:
Journal:
Publication Date:
Data Source:
PubMed

Record Created: