Fazirsiran for Adults With Alpha-1 Antitrypsin Deficiency Liver Disease: A Phase 2 Placebo Controlled Trial (SEQUOIA)

Clark, V. C., Strange, C., Strnad, P., Sanchez, A. J., Kwo, P., Pereira, V. M., van Hoek, B., Barjaktarevic, I., Corsico, A. G., Pons, M., Goldklang, M., Gray, M., Kuhn, B., Vargas, H. E., Vierling, J. M., Vuppalanchi, R., Brantly, M., Kappe, N., Chang, T., … Loomba, R. (2024). Fazirsiran for Adults With Alpha-1 Antitrypsin Deficiency Liver Disease: A Phase 2 Placebo Controlled Trial (SEQUOIA). Gastroenterology. https://doi.org/10.1053/j.gastro.2024.06.028
Authors:
Virginia Clark
Vitor Magno Pereira
Antonio J. Sanchez
Antonio J. Sanchez
Paul Y. Kwo
Vitor Magno Pereira
Bart van Hoek
Igor Barjaktarević
Angelo Corsico
Mònica Pons
Vitor Magno Pereira
Meagan Gray
Antonio J. Sanchez
Vitor Magno Pereira
Antonio J. Sanchez
Raj Vuppalanchi
Mark Brantly
Vitor Magno Pereira
Ting Chang
Thomas Schluep
Vitor Magno Pereira
James Hamilton
Javier San Martín
Vitor Magno Pereira
Affiliated Authors:
Vitor Magno Pereira
Author Keywords:
aat
alpha-1 antitrypsin deficiency
fazirsiran
liver disease
z-aat
Publication Type:
Article
Unique ID:
10.1053/j.gastro.2024.06.028
PMID:
Journal:
Publication Date:
Data Source:
OpenAlex

Record Created: