2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA Participants

Stimpson, G., Ramsey, D., Wolfe, A., Mayhew, A., Scoto, M., Baranello, G., Muni Lofra, R., Main, M., Milev, E., Coratti, G., Pane, M., Sansone, V., D’Amico, A., Bertini, E., Messina, S., Bruno, C., Albamonte, E., Mazzone, E. S., Montes, J., … Muntoni, F. (2023). 2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA Participants. Journal of Clinical Medicine, 12(5), 1920. https://doi.org/10.3390/jcm12051920
Authors:
Georgia Stimpson
Danielle Ramsey
Amy Wolfe
Anna Mayhew
Mariacristina Scoto
Giovanni Baranello
Robert Muni Lofra
Marion Main
Evelin Milev
Giorgia Coratti
Marika Pane
Valeria Sansone
Adele D’Amico
Enrico Bertini
Sonia Messina
Claudio Bruno
Emilio Albamonte
Elena Stacy Mazzone
Jacqueline Montes
Allan M. Glanzman
Zarazuela Zolkipli-Cunningham
Amy Pasternak
Tina Duong
Sally Dunaway Young
Matthew Civitello
Chiara Marini-Bettolo
John W. Day
Basil T. Darras
Darryl C. De Vivo
Richard S. Finkel
Eugenio Mercuri
Francesco Muntoni
Affiliated Authors:
Jacqueline Montes
Darryl C. De Vivo
Columbia Affiliation:
Subjects:
Gene Therapy for Spinal Muscular Atrophy (OpenAlex Topic)
Impact of Parenting Stress on Caregivers and Families (OpenAlex Topic)
Surgical Ventricular Reconstruction in Myocardial Infarction (OpenAlex Topic)
Author Keywords:
motor function
natural history
spinal muscular atrophy
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Publication Type:
Article
Unique ID:
10.3390/jcm12051920
DOI:
10.3390/jcm12051920
Journal:
Journal of Clinical Medicine
Publication Date:
Data Source:
Scopus
Source Link:
View Scopus Record
View OpenAlex Record
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