Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy

Foley, A. R., Yun, P., Leach, M. E., Neuhaus, S. B., Averion, G. V., Hu, Y., Hayes, L. H., Donkervoort, S., Jain, M. S., Waite, M., Parks, R., Bharucha-Goebel, D. X., Mayer, O. H., Zou, Y., Fink, M., DeCoster, J., Mendoza, C., Arévalo, C., Hausmann, R., … Bönnemann, C. G. (2024). Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy. Neurology Genetics, 10(3). https://doi.org/10.1212/nxg.0000000000200148
Authors:
A Reghan Foley
Pomi Yun
Meganne E Leach
Sarah B Neuhaus
Gilberto V Averion
Ying Hu
Leslie H Hayes
Sandra Donkervoort
Minal S Jain
Melissa Waite
Rebecca Parks
Diana X Bharucha-Goebel
Oscar H Mayer
Yaqun Zou
Margaret Fink
Jameice DeCoster
Christopher Mendoza
Cynthia Arévalo
Rudolf Hausmann
Diana Petraki
Ken Cheung
Carsten G Bönnemann
Affiliated Authors:
A Reghan Foley
Pomi Yun
Meganne E Leach
Sarah B Neuhaus
Gilberto V Averion
Ying Hu
Leslie H Hayes
Sandra Donkervoort
Minal S Jain
Melissa Waite
Rebecca Parks
Diana X Bharucha-Goebel
Oscar H Mayer
Yaqun Zou
Margaret Fink
Jameice DeCoster
Christopher Mendoza
Cynthia Arévalo
Rudolf Hausmann
Diana Petraki
Ken Cheung
Carsten G Bönnemann
Publication Type:
Article
Unique ID:
10.1212/nxg.0000000000200148
PMID:
Publication Date:
Data Source:
PubMed

Record Created: