Safety and efficacy of vanzacaftor–tezacaftor–deutivacaftor in adults with cystic fibrosis: randomised, double-blind, controlled, phase 2 trials

Uluer, A. Z., MacGregor, G., Azevedo, P., Indihar, V., Keating, C., Mall, M. A., McKone, E. F., Ramsey, B. W., Rowe, S. M., Rubenstein, R. C., Taylor-Cousar, J. L., Tullis, E., Yonker, L. M., Chu, C., Lam, A. P., Nair, N., Sosnay, P. R., Tian, S., Van Goor, F., … Wilson, J. (2023). Safety and efficacy of vanzacaftor–tezacaftor–deutivacaftor in adults with cystic fibrosis: randomised, double-blind, controlled, phase 2 trials. The Lancet Respiratory Medicine, 11(6), 550–562. https://doi.org/10.1016/s2213-2600(22)00504-5
Authors:
Ahmet Uluer
Gordon MacGregor
Pilar Azevedo
V. Indihar
Claire Keating
Marcus Mall
Edward F. McKone
Bonnie W. Ramsey
Steven M. Rowe
Ronald C. Rubenstein
Jennifer L. Taylor‐Cousar
Elizabeth Tullis
Lael M. Yonker
Chenghao Chu
Anna P. Lam
Nitin Nair
Patrick R. Sosnay
Simon Tian
Eva Van Braeckel
Lakshmi Viswanathan
David S. Goldfarb
Linda T. Wang
Yingmei Xi
Joanne Billings
Alex Horsley
Alex Horsley
E.F. Nash
Marleen Bakker
Renske van der Meer
Petrus Merkus
Christof J. Majoor
Karen McCoy
Joanne Billings
Krishna Pancham
James Tolle
Bryon Quick
Ahmet Uluer
Emily DiMango
Adupa P. Rao
Santiago Reyes
Ross C. Klingsberg
Celeste Barreto
Victor E. Ortega
Donna Beth Willey‐Courand
C. Schwarz
Sivagurunathan Sutharsan
Rainald Fischer
Janet Stocks
J. Duckers
Alex Horsley
Simon Doe
E.F. Nash
Marleen Bakker
Harry Heijerman
Renske van der Meer
Petrus Merkus
Christof J. Majoor
George M. Solomon
Christian A. Merlo
Jennifer Griffonnet
Joseph M. Pilewski
Jordan Dunitz
Saba Sheikh
Ronald C. Rubenstein
Daniel Rosenbluth
Theodore G. Liou
Maria Veronica Indihar
Krishna Pancham
Lael M. Yonker
Samya Z. Nasr
Jennifer Griffonnet
Cynthia Brown
Gregory S. Sawicki
Jennifer Ruddy
Emily DiMango
Bryan Garcia
Andrew T. Braun
Alex H. Gifford
Naima Mehdi
Maria Tupayachi Ortiz
Raksha Jain
Francisco J. Calimano
Jimmy Johannes
Cori Daines
Jason Fullmer
Joel Mermis
Christopher Barrios
Ngoc P. Ly
Brian Casserly
Stephan Eisenmann
Helge Hebestreit
Alexander Kiefer
Sivagurunathan Sutharsan
Rainald Fischer
Gordon MacGregor
D. Peckham
M.J. Ledson
Eva Van Braeckel
Petrus Merkus
Noel G. McElvaney
Affiliated Authors:
Ahmet Uluer
Gordon MacGregor
Pilar Azevedo
V. Indihar
Claire Keating
Edward F. McKone
Bonnie W. Ramsey
Steven M. Rowe
Ronald C. Rubenstein
Jennifer L. Taylor‐Cousar
Elizabeth Tullis
Lael M. Yonker
Anna P. Lam
Nitin Nair
Patrick R. Sosnay
Simon Tian
Eva Van Braeckel
Lakshmi Viswanathan
David S. Goldfarb
Linda T. Wang
Yingmei Xi
Joanne Billings
Alex Horsley
Alex Horsley
Joanne Billings
Ahmet Uluer
Alex Horsley
Simon Doe
Jennifer Griffonnet
Ronald C. Rubenstein
Maria Veronica Indihar
Lael M. Yonker
Jennifer Griffonnet
Jennifer Ruddy
Ngoc P. Ly
Alexander Kiefer
Gordon MacGregor
Publication Type:
Article
Unique ID:
10.1016/s2213-2600(22)00504-5
PMID:
Publication Date:
Data Source:
OpenAlex

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