P230 Safety update: Risdiplam clinical trial program for spinal muscular atrophy (SMA)

Baranello, G., Chiriboga, C., Servais, L., Darras, B., Day, J., Deconinck, N., Farrar, M., Finkel, R., Bertini, E., Kirschner, J., Rasson, M., Mazurkiewicz-Bełdzińska, M., Vlodavets, D., Bader-Weder, S., Gorni, K., Jaber, B., Yeung, W., Papp, G., Scalco, R., & Mercuri, E. (2023). P230 Safety update: Risdiplam clinical trial program for spinal muscular atrophy (SMA). Neuromuscular Disorders, 33, S92–S93. https://doi.org/10.1016/j.nmd.2023.07.112
Authors:
Giovanni Baranello
CA Chiriboga
Laurent Servais
Basil T. Darras
John Day
N. Deconinck
Michelle A. Farrar
R. Finkel
Enrico Bertini
Janbernd Kirschner
M. Rasson
Maria Carmela Pera
D. Vlodavets
Silvia Bader‐Weder
Ksenija Gorni
Birgit Jaber
Wai Yin Yeung
G. Papp
R. Scalco
Eugenio Mercuri
Affiliated Authors:
CA Chiriboga
Columbia Affiliation:
Subjects:
Gene Therapy for Spinal Muscular Atrophy (OpenAlex Topic)
RNA Methylation and Modification in Gene Expression (OpenAlex Topic)
Mechanisms and Applications of RNA Interference (OpenAlex Topic)
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Publication Type:
Article
Unique ID:
10.1016/j.nmd.2023.07.112
DOI:
10.1016/j.nmd.2023.07.112
Journal:
Neuromuscular Disorders
Publication Date:
Data Source:
OpenAlex
Source Link:
View OpenAlex Record

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