Todd, J. J., Lawal, T. A., Chrismer, I. C., Kokkinis, A., Grunseich, C., Jain, M. S., Waite, M. R., Biancavilla, V., Pocock, S., Brooks, K., Mendoza, C. J., Norato, G., Cheung, K., Riekhof, W., Varma, P., Colina-Prisco, C., Emile-Backer, M., Meilleur, K. G., Marks, A. R., … Mohassel, P. (2024). Rycal S48168 (ARM210) for RYR1-related myopathies: a phase one, open-label, dose-escalation trial. EClinicalMedicine, 68, 102433. https://doi.org/10.1016/j.eclinm.2024.102433
Publication Type:
Article
Unique ID:
10.1016/j.eclinm.2024.102433
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Data Source:
PubMed