Therapeutic Advances in Rare Disease

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Chehade, M., Furuta, G., Klion, A., Abonia, J. P., Aceves, S., Bose, P., Collins, M. H., Davis, C., Dellon, E. S., Eickel, G., Falk, G., Gupta, S., Hiremath, G., Howard, A., Jensen, E. T., Kesh, S., Khoury, P., Kocher, K., Kodroff, E., … Bailey, D. D. (2023). Enhancing diversity, equity, inclusion, and accessibility in eosinophilic gastrointestinal disease research: the consortium for eosinophilic gastrointestinal disease researchers’ journey. Therapeutic Advances in Rare Disease, 4. https://doi.org/10.1177/26330040231180895
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Sparks, J., Michelassi, F., Thompson, J. L. P., Buchsbaum, R., Pires, N., DeRosa, J. T., Engelstad, K., DiMauro, S., Akman, H. O., & Hirano, M. (2024). A United States-based patient-reported adult polyglucosan body disease registry: initial results. Therapeutic Advances in Rare Disease, 5. https://doi.org/10.1177/26330040241227452
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Heilmann, R., Pfalzer, A., Bichell, T. J., Terala, A., Campbell, A., Taatjes, D., Ghoumid, J., Grueter, C., Bain, J., Strich, R., Dias, V., Sokorai, K., Seaver, N., Sexton, K., & Boychuck, K. (2024). The MED13L Foundation strategic research plan: a roadmap to the future. Therapeutic Advances in Rare Disease, 5. https://doi.org/10.1177/26330040241290252
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