Dependovirus
Hammer, D. R., Voruz, F., Aksit, A., Breil, E., Rousset, F., Senn, P., Ilmjärv, S., Olson, E. S., Lalwani, A. K., & Kysar, J. W. (2025). Novel dual-lumen microneedle delivers adeno-associated viral vectors in the guinea pig inner ear via the round window membrane. Biomedical Microdevices, 27(2). https://doi.org/10.1007/s10544-025-00751-4
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Columbia Affiliation
Li, Y., Yang, R. R., Li, Y. S., Hsu, C. W., Jenny, L. A., Kong, Y., Ruan, M. Z., Sparrow, J. R., & Tsang, S. H. (2024). Evaluating precision medicine approaches for gene therapy in patient-specific cellular models of Bietti crystalline dystrophy. JCI insight, 9(16), e177231. https://doi.org/10.1172/jci.insight.177231
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Columbia Affiliation
Shamshad, A., Kang, C., Jenny, L. A., Persad-Paisley, E. M., & Tsang, S. H. (2023). Translatability barriers between preclinical and clinical trials of AAV gene therapy in inherited retinal diseases. Vision Research, 210, 108258. https://doi.org/10.1016/j.visres.2023.108258
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Columbia Affiliation