Dunaway Young, S., Montes, J., Glanzman, A. M., Gee, R., Day, J. W., Finkel, R. S., Darras, B. T., De Vivo, D. C., Gambino, G., Foster, R., Wong, J., Garafalo, S., & Berger, Z. (2023). Nusinersen Treatment of Children with Later-Onset Spinal Muscular Atrophy and Scoliosis Is Associated with Improvements or Stabilization of Motor Function. Journal of Clinical Medicine, 12(15), 4901. https://doi.org/10.3390/jcm12154901
Subjects:
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Etiology and Management of Abdominal Wall Defects
(OpenAlex Topic)
RNA Methylation and Modification in Gene Expression
(OpenAlex Topic)
Publication Type:
Article
Unique ID:
10.3390/jcm12154901
DOI:
Journal:
Publication Date:
Data Source:
Scopus
Source Link: