Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy

Errico, F., Marino, C., Grimaldi, M., Nuzzo, T., Bassareo, V., Valsecchi, V., Panicucci, C., Di Schiavi, E., Mazza, T., Bruno, C., D’Amico, A., Carta, M., D’Ursi, A. M., Bertini, E., Pellizzoni, L., & Usiello, A. (2022). Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy. Biomolecules, 12(10), 1431. https://doi.org/10.3390/biom12101431
Authors:
Francesco Errico
Carmen Marino
Manuela Grimaldi
Tommaso Nuzzo
Valentina Bassareo
Valeria Valsecchi
Chiara Panicucci
Elia Di Schiavi
Tommaso Mazza
Claudio Bruno
Adele D’Amico
Manolo Carta
Anna Maria D’Ursi
Enrico Bertini
Livio Pellizzoni
Alessandro Usiello
Affiliated Authors:
Livio Pellizzoni
Author Keywords:
spinal muscular atrophy (sma)
survival motor neuron (smn)
nusinersen
cerebrospinal fluid (csf)
nuclear magnetic resonance (nmr)
Publication Type:
Article
Unique ID:
10.3390/biom12101431
PMID:
Journal:
Publication Date:
Data Source:
Scopus

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