DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results

Finkel, R. S., Day, J. W., Pascual Pascual, S. I., Ryan, M. M., Mercuri, E., De Vivo, D. C., Montes, J., Gurgel-Giannetti, J., Monine, M., Gambino, G., Makepeace, C., Foster, R., Berger, Z., & DEVOTE Study Group (2023). DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results. Journal of neuromuscular diseases, 10(5), 813–823. https://doi.org/10.3233/JND-221667

Authors:
Richard S. Finkel
John W. Day
Samuel Ignacio Pascual Pascual
Monique M. Ryan
Eugenio Mercuri
Darryl C. De Vivo
Jacqueline Montes
Juliana Gurgel-Giannetti
Michael Monine
Giulia Gambino
Corinne Makepeace
Richard Foster
Zdenek Berger
Affiliated Authors:
Darryl C. De Vivo
Jacqueline Montes
Subjects:
Author Keywords:
spinal muscular atrophy
nusinersen
safety
pharmacokinetics
Publication Type:
Article
Unique ID:
10.3233/JND-221667
PMID:
Publication Date:
Data Source:
Scopus

Record Created: