Finkel, R. S., Day, J. W., Pascual Pascual, S. I., Ryan, M. M., Mercuri, E., De Vivo, D. C., Montes, J., Gurgel-Giannetti, J., Monine, M., Gambino, G., Makepeace, C., Foster, R., Berger, Z., & DEVOTE Study Group (2023). DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results. Journal of neuromuscular diseases, 10(5), 813–823. https://doi.org/10.3233/JND-221667
Subjects:
Muscular Atrophy, Spinal
(MeSH)
Publication Type:
Article
Unique ID:
10.3233/JND-221667
PMID:
DOI:
Journal:
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Data Source:
Scopus