Pasternak, A., McDermott, M. P., Montes, J., Glanzman, A. M., Coratti, G., Dunaway Young, S., Duong, T. T., Martens, W. B., Day, J. W., Zolkipli-Cunningham, Z., Sansone, V. A., D’Amico, A., Messina, S., Bruno, C., Mercuri, E., De Vivo, D. C., & Darras, B. T. (2025). Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts. Neurology, 105(2). https://doi.org/10.1212/wnl.0000000000213839
Subjects:
Oligonucleotides
(MeSH)
Muscular Atrophy, Spinal
(MeSH)
Publication Type:
Article
Unique ID:
10.1212/wnl.0000000000213839
PMID:
Journal:
Publication Date:
Data Source:
PubMed
Source Link: