Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts

Pasternak, A., McDermott, M. P., Montes, J., Glanzman, A. M., Coratti, G., Dunaway Young, S., Duong, T. T., Martens, W. B., Day, J. W., Zolkipli-Cunningham, Z., Sansone, V. A., D’Amico, A., Messina, S., Bruno, C., Mercuri, E., De Vivo, D. C., & Darras, B. T. (2025). Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts. Neurology, 105(2). https://doi.org/10.1212/wnl.0000000000213839
Authors:
Amy Pasternak
Michael P McDermott
Jacqueline Montes
Allan M Glanzman
Giorgia Coratti
Sally Dunaway Young
Trinh Tina Duong
William B Martens
John W Day
Zarazuela Zolkipli-Cunningham
Valeria Ada Sansone
Adele D'Amico
Sonia Messina
Claudio Bruno
Eugenio Mercuri
Darryl C De Vivo
Basil T Darras
Affiliated Authors:
Jacqueline Montes
Darryl C De Vivo
Subjects:
Publication Type:
Article
Unique ID:
10.1212/wnl.0000000000213839
PMID:
Journal:
Publication Date:
Data Source:
PubMed

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