Trucco, F., Ridout, D., Weststrate, H., Scoto, M., Rohwer, A., Coratti, G., Main, M. L., Mayhew, A. G., Montes, J., De Sanctis, R., Pane, M., Pera, M. C., Sansone, V. A., Albamonte, E., D’Amico, A., Bruno, C., Messina, S. S., Childs, A.-M., … Willis, T. (2024). Therapeutic Role of Nusinersen on Respiratory Progression in Pediatric Patients With Spinal Muscular Atrophy Type 2 and Nonambulant Type 3. Neurology Clinical Practice, 14(3). https://doi.org/10.1212/cpj.0000000000200298
Publication Type:
Article
Unique ID:
10.1212/cpj.0000000000200298
PMID:
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Data Source:
PubMed