Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia

Locatelli, F., Lang, P., Li, A., Corbacioglu, S., de la Fuente, J., Wall, D. A., Liem, R., Meisel, R., Mapara, M. Y., Shah, A. J., Cappellini, M. D. D., Kattamis, A., Sheth, S., Bobruff, Y., Bower, L., Zhang, L., Sharma, A., Song, Y., Hobbs, W., & Frangoul, H. (2022). Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia. Blood, 140(Supplement 1), 4899–4901. https://doi.org/10.1182/blood-2022-166881
Authors:
Franco Locatelli
Peter Lang
Amanda Li
Selim Corbacioglu
Josu de la Fuente
Donna A. Wall
Robert I. Liem
Roland Meisel
Markus Y. Mapara
Ami J. Shah
Maria Domenica Cappellini
Antonis Kattamis
Sujit Sheth
Yael Bobruff
Laura Bower
Lanju Zhang
Anjali Sharma
Yang Song
William Hobbs
Haydar Frangoul
Affiliated Authors:
Markus Y. Mapara
Publication Type:
Article
Unique ID:
10.1182/blood-2022-166881
Journal:
Publication Date:
Data Source:
OpenAlex

Record Created: