Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Severe Sickle Cell Disease

Frangoul, H., Locatelli, F., Bhatia, M., Mapara, M. Y., Molinari, L., Sharma, A., Lobitz, S., de Montalembert, M., Rondelli, D., Steinberg, M., Walters, M. C., Imren, S., Zhang, L., Sharma, A., Song, Y., Simard, C., Hobbs, W., & Grupp, S. (2022). Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Severe Sickle Cell Disease. Blood, 140(Supplement 1), 29–31. https://doi.org/10.1182/blood-2022-162353
Authors:
Haydar Frangoul
Franco Locatelli
Monica Bhatia
Markus Y. Mapara
Lyndsay Molinari
Akshay Sharma
Stephan Lobitz
Mariane de Montalembert
Damiano Rondelli
Martin H. Steinberg
Mark C. Walters
Suzan Imren
Lanju Zhang
Anjali Sharma
Yang Song
C Simard
William Hobbs
Stephen Grupp
Affiliated Authors:
Monica Bhatia
Markus Y. Mapara
Publication Type:
Article
Unique ID:
10.1182/blood-2022-162353
Journal:
Publication Date:
Data Source:
OpenAlex

Record Created: