Longitudinal Assessment of 4-Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen

Coratti, G., Bovis, F., Pane, M., Pasternak, A., Albamonte, E., Mizzoni, I., Glanzman, A. M., Morando, S., Montes, J., Cavallina, I., Dunaway Young, S., Duong, T., Rolle, E., Civitello, M., De Sanctis, R., Bravetti, C., Ricci, F., Gadaleta, G., … Mongini, T. (2025). Longitudinal Assessment of 4‐Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen. European Journal of Neurology, 32(7). Portico. https://doi.org/10.1111/ene.70268
Authors:
Giorgia Coratti
Francesca Bovis
Marika Pane
Amy Pasternak
Emilio Albamonte
Irene Mizzoni
Allan M Glanzman
Simone Morando
Jacqueline Montes
Ilaria Cavallina
Sally Dunaway Young
Tina Duong
Enrica Rolle
Matthew Civitello
Roberto De Sanctis
Chiara Bravetti
Federica Ricci
Giulio Gadaleta
Tiziana Mongini
Maria Sframeli
Maria Carmela Pera
Sonia Messina
Adele D'Amico
Michela Catteruccia
Noemi Brolatti
Michio Hirano
Zarazuela Zolkipli-Cunningham
Basil T Darras
Enrico Bertini
Claudio Bruno
John Day
Valeria A Sansone
Richard S Finkel
Eugenio Mercuri
Affiliated Authors:
Jacqueline Montes
Michio Hirano
Author Keywords:
hammersmith functional motor scale expanded
long term results
motor function
nusinersen
spinal muscular atrophy
Publication Type:
Article
Unique ID:
10.1111/ene.70268
PMID:
Publication Date:
Data Source:
PubMed

Record Created: