Coratti, G., Bovis, F., Pane, M., Pasternak, A., Albamonte, E., Mizzoni, I., Glanzman, A. M., Morando, S., Montes, J., Cavallina, I., Dunaway Young, S., Duong, T., Rolle, E., Civitello, M., De Sanctis, R., Bravetti, C., Ricci, F., Gadaleta, G., … Mongini, T. (2025). Longitudinal Assessment of 4‐Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen. European Journal of Neurology, 32(7). Portico. https://doi.org/10.1111/ene.70268
Subjects:
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
RNA Methylation and Modification in Gene Expression
(OpenAlex Topic)
Regulation of RNA Processing and Function
(OpenAlex Topic)
Oligonucleotides
(MeSH)
Publication Type:
Article
Unique ID:
10.1111/ene.70268
PMID:
DOI:
Journal:
Publication Date:
Data Source:
PubMed
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