Central Nervous System-Targeted Gene Therapy for the Treatment of Neurocognitive Deficits in Mucopolysaccharidosis Type II Mice

Chen, G., Zhan, X., Gao, X., Yi, M., Liang, H., Chen, Y., Lin, Q., Yang, J., Hou, S., Maegawa, G., & Zhang, H. (2025). Central Nervous System-Targeted Gene Therapy for the Treatment of Neurocognitive Deficits in Mucopolysaccharidosis Type II Mice. Human Gene Therapy. https://doi.org/10.1089/hum.2024.229
Authors:
Guoqing Chen
Xia Zhan
Xiaolan Gao
Mengni Yi
Huan Liang
Yixiong Chen
Qing Lin
Jun Yang
Shule Hou
Gustavo Maegawa
Huiwen Zhang
Affiliated Authors:
Gustavo Maegawa
Author Keywords:
aav
gene therapy
mucopolysaccharidosis type ii
neurocognitive function
Publication Type:
Article
Unique ID:
10.1089/hum.2024.229
PMID:
Publication Date:
Data Source:
PubMed

Record Created: