Exagamglogene Autotemcel for Severe Sickle Cell Disease

Frangoul, H., Locatelli, F., Sharma, A., Bhatia, M., Mapara, M., Molinari, L., Wall, D., Liem, R. I., Telfer, P., Shah, A. J., Cavazzana, M., Corbacioglu, S., Rondelli, D., Meisel, R., Dedeken, L., Lobitz, S., de Montalembert, M., Steinberg, M. H., Walters, M. C., … Grupp, S. A. (2024). Exagamglogene Autotemcel for Severe Sickle Cell Disease. New England Journal of Medicine, 390(18), 1649–1662. https://doi.org/10.1056/nejmoa2309676
Authors:
Haydar Frangoul
Franco Locatelli
Akshay Sharma
Monica Bhatia
Markus Mapara
Lyndsay Molinari
Donna Wall
Robert I Liem
Paul Telfer
Ami J Shah
Marina Cavazzana
Selim Corbacioglu
Damiano Rondelli
Roland Meisel
Laurence Dedeken
Stephan Lobitz
Mariane de Montalembert
Martin H Steinberg
Mark C Walters
Michael J Eckrich
Suzan Imren
Laura Bower
Christopher Simard
Weiyu Zhou
Fengjuan Xuan
Phuong Khanh Morrow
William E Hobbs
Stephan A Grupp
Affiliated Authors:
Haydar Frangoul
Franco Locatelli
Akshay Sharma
Monica Bhatia
Markus Mapara
Lyndsay Molinari
Donna Wall
Robert I Liem
Paul Telfer
Ami J Shah
Marina Cavazzana
Selim Corbacioglu
Damiano Rondelli
Roland Meisel
Laurence Dedeken
Stephan Lobitz
Mariane de Montalembert
Martin H Steinberg
Mark C Walters
Michael J Eckrich
Suzan Imren
Laura Bower
Christopher Simard
Weiyu Zhou
Fengjuan Xuan
Phuong Khanh Morrow
William E Hobbs
Stephan A Grupp
Publication Type:
Article
Unique ID:
10.1056/nejmoa2309676
PMID:
Publication Date:
Data Source:
PubMed

Record Created: