Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis

Maurer, M. S., Kale, P., Fontana, M., Berk, J. L., Grogan, M., Gustafsson, F., Hung, R. R., Gottlieb, R. L., Damy, T., González-Duarte, A., Sarswat, N., Sekijima, Y., Tahara, N., Taylor, M. S., Kubanek, M., Donal, E., Palecek, T., Tsujita, K., Tang, W. H. W., … Gillmore, J. D. (2023). Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis. New England Journal of Medicine, 389(17), 1553–1565. https://doi.org/10.1056/nejmoa2300757
Authors:
Mathew S Maurer
Parag Kale
Marianna Fontana
John L Berk
Martha Grogan
Finn Gustafsson
Rebecca R Hung
Robert L Gottlieb
Thibaud Damy
Alejandra González-Duarte
Nitasha Sarswat
Yoshiki Sekijima
Nobuhiro Tahara
Mark S Taylor
Milos Kubanek
Erwan Donal
Tomas Palecek
Kenichi Tsujita
W H Wilson Tang
Wen-Chung Yu
Laura Obici
Marcus Simões
Fábio Fernandes
Steen Hvitfeldt Poulsen
Igor Diemberger
Federico Perfetto
Scott D Solomon
Marcelo Di Carli
Prajakta Badri
Matthew T White
Jihong Chen
Elena Yureneva
Marianne T Sweetser
Patrick Y Jay
Pushkal P Garg
John Vest
Julian D Gillmore
Affiliated Authors:
Mathew S Maurer
Parag Kale
Marianna Fontana
John L Berk
Martha Grogan
Finn Gustafsson
Rebecca R Hung
Robert L Gottlieb
Thibaud Damy
Alejandra González-Duarte
Nitasha Sarswat
Yoshiki Sekijima
Nobuhiro Tahara
Mark S Taylor
Milos Kubanek
Erwan Donal
Tomas Palecek
Kenichi Tsujita
W H Wilson Tang
Wen-Chung Yu
Laura Obici
Marcus Simões
Fábio Fernandes
Steen Hvitfeldt Poulsen
Igor Diemberger
Federico Perfetto
Scott D Solomon
Marcelo Di Carli
Prajakta Badri
Matthew T White
Jihong Chen
Elena Yureneva
Marianne T Sweetser
Patrick Y Jay
Pushkal P Garg
John Vest
Julian D Gillmore
Subjects:
Publication Type:
Article
Unique ID:
10.1056/nejmoa2300757
PMID:
Publication Date:
Data Source:
PubMed

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