Lumpkin, C. J., Harris, A. W., Connell, A. J., Kirk, R. W., Whiting, J. A., Saieva, L., Pellizzoni, L., Burghes, A. H. M., & Butchbach, M. E. R. (2023). Evaluation of the orally bioavailable 4-phenylbutyrate-tethered trichostatin A analogue AR42 in models of spinal muscular atrophy. Scientific Reports, 13(1). https://doi.org/10.1038/s41598-023-37496-0
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10.1038/s41598-023-37496-0
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