Treatment with THI, an inhibitor of sphingosine-1-phosphate lyase, modulates glycosphingolipid metabolism and results therapeutically effective in experimental models of Huntington's disease

Pepe, G., Capocci, L., Marracino, F., Realini, N., Lenzi, P., Martinello, K., Bovier, T. F., Bichell, T. J., Scarselli, P., Di Cicco, C., Bowman, A. B., Digilio, F. A., Fucile, S., Fornai, F., Armirotti, A., Parlato, R., Di Pardo, A., & Maglione, V. (2023). Treatment with THI, an inhibitor of sphingosine-1-phosphate lyase, modulates glycosphingolipid metabolism and results therapeutically effective in experimental models of Huntington’s disease. Molecular Therapy, 31(1), 282–299. https://doi.org/10.1016/j.ymthe.2022.09.004
Authors:
Giuseppe Pepe
Luca Capocci
Federico Marracino
Natalia Realini
Paola Lenzi
Katiuscia Martinello
Tiziana Francesca Bovier
Terry Jo Bichell
Pamela Scarselli
Clotilde Di Cicco
Aaron B Bowman
Filomena A Digilio
Sergio Fucile
Francesco Fornai
Andrea Armirotti
Rosanna Parlato
Alba Di Pardo
Vittorio Maglione
Affiliated Authors:
Tiziana Francesca Bovier
Subjects:
Author Keywords:
glucosylceramide
hd
htt
neurodegeneration
neuroprotection
therapeutics
thi
Publication Type:
Article
Unique ID:
10.1016/j.ymthe.2022.09.004
PMID:
Publication Date:
Data Source:
PubMed

Record Created: