Changes in abilities over the initial 12 months of nusinersen treatment for type II SMA

Coratti, G., Civitello, M., Rohwer, A., Salmin, F., Glanzman, A. M., Montes, J., Pasternak, A., De Sanctis, R., Young, S. D., Duong, T., Mizzoni, I., Milev, E., Sframeli, M., Morando, S., Albamonte, E., D’Amico, A., Brolatti, N., Pane, M., Scoto, M., … Mercuri, E. (2024). Changes in abilities over the initial 12 months of nusinersen treatment for type II SMA. Neuromuscular Disorders, 41, 42–50. https://doi.org/10.1016/j.nmd.2024.05.003
Authors:
Giorgia Coratti
Matthew Civitello
Annemarie Rohwer
Francesca Salmin
Allan M Glanzman
Jaqueline Montes
Amy Pasternak
Roberto De Sanctis
Sally Dunaway Young
Tina Duong
Irene Mizzoni
Evelin Milev
Maria Sframeli
Simone Morando
Emilio Albamonte
Adele D'Amico
Noemi Brolatti
Marika Pane
Mariacristina Scoto
Sonia Messina
Michio Hirano
Zarazuela Zolkipli-Cunningham
Basil T Darras
Enrico Bertini
Claudio Bruno
Valeria A Sansone
John Day
Giovanni Baranello
Maria Carmela Pera
Francesco Muntoni
Richard Finkel
Eugenio Mercuri
Affiliated Authors:
Jaqueline Montes
Michio Hirano
Author Keywords:
hammersmith functional motor scale expanded
motor function
nusinersen
shift analysis
spinal muscular atrophy
treatment effect
hammersmith functional motor scale
expanded
Publication Type:
Article
Unique ID:
10.1016/j.nmd.2024.05.003
PMID:
Publication Date:
Data Source:
PubMed

Record Created: