Crawford, T., Darras, B., Day, J., De Vivo, D., Mercuri, E., Nascimento, A., Mazzone, E., Waugh, A., Song, G., Evans, R., & Marantz, J. (2023). P224 Effect of apitegromab on motor function at 36 months in patients with nonambulatory spinal muscular atrophy aged 2-12 years old. Neuromuscular Disorders, 33, S91. https://doi.org/10.1016/j.nmd.2023.07.106
Subjects:
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Molecular Basis of Rett Syndrome and Related Disorders
(OpenAlex Topic)
Publication Type:
Article
Unique ID:
10.1016/j.nmd.2023.07.106
Journal:
Publication Date:
Data Source:
OpenAlex
Source Link: