Kim, J.-K., Jha, N. N., Awano, T., Caine, C., Gollapalli, K., Welby, E., Kim, S.-S., Fuentes-Moliz, A., Wang, X., Feng, Z., Sera, F., Takeda, T., Homma, S., Ko, C.-P., Tabares, L., Ebert, A. D., Rich, M. M., & Monani, U. R. (2023). A spinal muscular atrophy modifier implicates the SMN protein in SNARE complex assembly at neuromuscular synapses. Neuron, 111(9), 1423-1439.e4. https://doi.org/10.1016/j.neuron.2023.02.004
Columbia Affiliation:
Subjects:
Muscular Atrophy, Spinal
(MeSH)
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Regulation of RNA Processing and Function
(OpenAlex Topic)
RNA Methylation and Modification in Gene Expression
(OpenAlex Topic)
Publication Type:
Article
Unique ID:
10.1016/j.neuron.2023.02.004
PMID:
Journal:
Publication Date:
Data Source:
OpenAlex
Source Link: