Chiriboga, C. A., Bruno, C., Duong, T., Fischer, D., Mercuri, E., Kirschner, J., Kostera-Pruszczyk, A., Jaber, B., Gorni, K., Kletzl, H., Carruthers, I., Martin, C., Warren, F., Scalco, R. S., Wagner, K. R., Muntoni, F., Deconinck, N., Balikova, I., … Collado, J. (2023). Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study. Neurology and Therapy, 12(2), 543–557. https://doi.org/10.1007/s40120-023-00444-1
Subjects:
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
RNA Methylation and Modification in Gene Expression
(OpenAlex Topic)
Aetiology, Diagnosis, and Management of Myocarditis
(OpenAlex Topic)
Publication Type:
Article
Unique ID:
10.1007/s40120-023-00444-1
PMID:
Journal:
Publication Date:
Data Source:
PubMed
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