JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam

Chiriboga, C. A., Bruno, C., Duong, T., Fischer, D., Mercuri, E., Kirschner, J., Kostera-Pruszczyk, A., Jaber, B., Gorni, K., Kletzl, H., Carruthers, I., Martin, C., Scalco, R. S., Fontoura, P., & Muntoni, F. (2024). JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam. Journal of Neurology, 271(8), 4871–4884. https://doi.org/10.1007/s00415-024-12318-z

Authors:

Claudia A. Chiriboga

Claudio Bruno

Tina Duong

Dirk Fischer

Eugenio Mercuri

Janbernd Kirschner

Anna Kostera‐Pruszczyk

Birgit Jaber

Ksenija Gorni

Heidemarie Kletzl

Imogen Carruthers