Triheptanoin Did Not Show Benefit versus Placebo for the Treatment of Paroxysmal Movement Disorders in Glut1 Deficiency Syndrome: Results of a Randomized Phase 3 Study

De Giorgis, V., Bhatia, K. P., Boespflug‐Tanguy, O., Gras, D., Marina, A. D., Desurkar, A., Toledo, M., Miller, I., Rotstein, M., Schneider, S. A., Tarquinio, D. C., Weber, Y., Brandabur, M., Mayhew, J., Koutsoukos, T., & De Vivo, D. C. (2024). Triheptanoin Did Not Show Benefit versus Placebo for the Treatment of Paroxysmal Movement Disorders in Glut1 Deficiency Syndrome: Results of a Randomized Phase 3 Study. Movement Disorders, 39(8), 1386–1396. Portico. https://doi.org/10.1002/mds.29822
Authors:
Valentina De Giorgis
Kailash P. Bhatia
Odile Boespflug-Tanguy
Domitille Gras
Adela Della Marina
Archana Desurkar
Manuel Toledo
Ian Miller
Michael Rotstein
Susanne A. Schneider
Daniel C. Tarquinio
Yvonne Weber
Melanie Brandabur
Jill Mayhew
Tony Koutsoukos
Darryl C. De Vivo
Affiliated Authors:
Darryl C. De Vivo
Author Keywords:
glucose transporter type 1 deficiency syndrome
paroxysmal movement disorder
phase 3
triheptanoin
ux007
Publication Type:
Article
Unique ID:
10.1002/mds.29822
PMID:
Publication Date:
Data Source:
Web of Science

Record Created: