Combination disease-modifying treatment in spinal muscular atrophy: A proposed classification

Proud, C. M., Mercuri, E., Finkel, R. S., Kirschner, J., De Vivo, D. C., Muntoni, F., Saito, K., Tizzano, E. F., Desguerre, I., Quijano‐Roy, S., Benguerba, K., Raju, D., Faulkner, E., & Servais, L. (2023). Combination disease‐modifying treatment in spinal muscular atrophy: A proposed classification. Annals of Clinical and Translational Neurology, 10(11), 2155–2160. Portico. https://doi.org/10.1002/acn3.51889
Authors:
Crystal M Proud
Eugenio Mercuri
Richard S Finkel
Janbernd Kirschner
Darryl C De Vivo
Francesco Muntoni
Kayoko Saito
Eduardo F Tizzano
Isabelle Desguerre
Susana Quijano-Roy
Kamal Benguerba
Dheeraj Raju
Eric Faulkner
Laurent Servais
Affiliated Authors:
Darryl C De Vivo
Publication Type:
Article
Unique ID:
10.1002/acn3.51889
PMID:
Publication Date:
Data Source:
PubMed

Record Created: