Proud, C. M., Mercuri, E., Finkel, R. S., Kirschner, J., De Vivo, D. C., Muntoni, F., Saito, K., Tizzano, E. F., Desguerre, I., Quijano‐Roy, S., Benguerba, K., Raju, D., Faulkner, E., & Servais, L. (2023). Combination disease‐modifying treatment in spinal muscular atrophy: A proposed classification. Annals of Clinical and Translational Neurology, 10(11), 2155–2160. Portico. https://doi.org/10.1002/acn3.51889
Subjects:
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Etiology and Management of Abdominal Wall Defects
(OpenAlex Topic)
Muscular Atrophy, Spinal
(MeSH)
Publication Type:
Article
Unique ID:
10.1002/acn3.51889
PMID:
DOI:
Publication Date:
Data Source:
PubMed
Source Link: