Nusinersen in pediatric and adult patients with type III spinal muscular atrophy

Pera, M. C., Coratti, G., Bovis, F., Pane, M., Pasternak, A., Montes, J., Sansone, V. A., Dunaway Young, S., Duong, T., Messina, S., Mizzoni, I., D’Amico, A., Civitello, M., Glanzman, A. M., Bruno, C., Salmin, F., Morando, S., De Sanctis, R., … Sframeli, M. (2021). Nusinersen in pediatric and adult patients with type III spinal muscular atrophy. Annals of Clinical and Translational Neurology, 8(8), 1622–1634. Portico. https://doi.org/10.1002/acn3.51411
Authors:
Maria Carmela Pera
Giorgia Coratti
Francesca Bovis
Marika Pane
Amy Pasternak
Jacqueline Montes
Valeria A. Sansone
Sally Dunaway Young
Tina Duong
Sonia Messina
Irene Mizzoni
Adele D’Amico
Matthew Civitello
Allan M. Glanzman
Claudio Bruno
Francesca Salmin
Simone Morando
Roberto De Sanctis
Maria Sframeli
Laura Antonaci
Anna Lia Frongia
Annemarie Rohwer
Mariacristina Scoto
Darryl C. De Vivo
Basil T. Darras
John Day
William Martens
Katia A. Patanella
Enrico Bertini
Francesco Muntoni
Richard Finkel
Eugenio Mercuri
Affiliated Authors:
Jacqueline Montes
Darryl C. De Vivo
Publication Type:
Article
Unique ID:
10.1002/acn3.51411
PMID:
Publication Date:
Data Source:
Scopus

Record Created: