CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

Hayden, D., Lai, P.-Y., Donahue, R. A., Chen, H.-W., Wang, J., Mathai, N., Lopes, G., McCaffrey, A., Scalia, J., Luppino, S., Lagier-Tourenne, C., Sadri-Vakili, G., Kolb, S., Heintzman, S., Sufit, R., Szymanski, A., Jenkins, L., … Martin, A. (2025). CNM-Au8 in Amyotrophic Lateral Sclerosis. JAMA. https://doi.org/10.1001/jama.2024.27643
Authors:
James D Berry
Nicholas J Maragakis
Eric A Macklin
Lori B Chibnik
Melanie Quintana
Benjamin R Saville
Michelle A Detry
Matteo Vestrucci
Joseph Marion
Anna McGlothlin
Elijah W Stommel
Marianne Chase
Lindsay Pothier
Brittney A Harkey
Hong Yu
Alex Sherman
Jeremy Shefner
Meghan Hall
Gale Kittle
Suma Babu
Jinsy Andrews
Derek D'Agostino
Eric Tustison
Erica Scirocco
Elisa Giacomelli
Gustavo Alameda
Eduardo Locatelli
Doreen Ho
Adam Quick
Senda Ajroud-Driss
Jonathan Katz
Daragh Heitzman
Stanley H Appel
Sheetal Shroff
Kevin J Felice
Zachary Simmons
Timothy Miller
Nicholas Olney
Michael D Weiss
Stephen A Goutman
Joseph Americo Fernandes
Omar Jawdat
Margaret Ayo Owegi
Laura Foster
Tuan Vu
Hristelina Ilieva
Daniel S Newman
Ximena Arcila-Londono
Carlayne Jackson
Shafeeq Ladha
Terry Heiman-Patterson
James Caress
Andrea Swenson
Amanda Peltier
Richard Lewis
Dominic Fee
Matthew Elliott
Richard Bedlack
Edward J Kasarskis
Lauren Elman
Jeffrey Rosenfeld
David Walk
Courtney E McIlduff
Paul Twydell
Eufrosina Young
Kristin Johnson
Kourosh Rezania
Namita A Goyal
Jeffrey A Cohen
Michael Benatar
Vovanti Jones
Jonathan Glass
Jaimin Shah
Said R Beydoun
James P Wymer
Lindsay Zilliox
Shakti Nayar
Gary L Pattee
Jennifer Martinez-Thompson
Austin Rynders
Jacob Evan
Jeremy Evan
Alan Hartford
Marjan Sepassi
Karen S Ho
Robert Glanzman
Benjamin Greenberg
Michael T Hotchkin
Sabrina Paganoni
Merit E Cudkowicz
Affiliated Authors:
Jinsy Andrews
Publication Type:
Article
Unique ID:
10.1001/jama.2024.27643
PMID:
Publication Date:
Data Source:
PubMed

Record Created: