Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series

Shneider, N. A., Harms, M. B., Korobeynikov, V. A., Rifai, O. M., Hoover, B. N., Harrington, E. A., Aziz-Zaman, S., Singleton, J., Jamil, A., Madan, V. R., Lee, I., Andrews, J. A., Smiley, R. M., Alam, M. M., Black, L. E., Shin, M., Watts, J. K., Walk, D., Newman, D., … Bennett, C. F. (2025). Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series. The Lancet. https://doi.org/10.1016/s0140-6736(25)00513-6
Authors:
Neil A Shneider
Matthew B Harms
Vlad A Korobeynikov
Olivia M Rifai
Benjamin N Hoover
Elizabeth A Harrington
Sonya Aziz-Zaman
Jessica Singleton
Arish Jamil
Vikram R Madan
Ikjae Lee
Jinsy A Andrews
Richard M Smiley
Mahabub M Alam
Lauren E Black
Minwook Shin
Jonathan K Watts
David Walk
Daniel Newman
Robert M Pascuzzi
Markus Weber
Christoph Neuwirth
Sandrine Da Cruz
Armand Soriano
Roger Lane
Scott Henry
Joel Mathews
Paymaan Jafar-Nejad
Dan Norris
Frank Rigo
Robert H Brown
Stephan Miller
Rebecca Crean
C Frank Bennett
Affiliated Authors:
Neil A Shneider
Matthew B Harms
Vlad A Korobeynikov
Olivia M Rifai
Benjamin N Hoover
Elizabeth A Harrington
Sonya Aziz-Zaman
Jessica Singleton
Arish Jamil
Vikram R Madan
Ikjae Lee
Jinsy A Andrews
Richard M Smiley
Mahabub M Alam
Columbia Affiliation:
elink
Publication Type:
Article
Unique ID:
10.1016/s0140-6736(25)00513-6
PMID:
40414239
DOI:
10.1016/s0140-6736(25)00513-6
Journal:
Lancet
Publication Date:
Data Source:
PubMed
Source Link:
View PubMed Record
View Scopus Record

Record Created: