Aguilar-González, A., González-Correa, J. E., Barriocanal-Casado, E., Ramos-Hernández, I., Lerma-Juárez, M. A., Greco, S., Rodríguez-Sevilla, J. J., Molina-Estévez, F. J., Montalvo-Romeral, V., Ronzitti, G., Sánchez-Martín, R. M., Martín, F., & Muñoz, P. (2022). Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies. International Journal of Molecular Sciences, 23(11), 6298. https://doi.org/10.3390/ijms23116298
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10.3390/ijms23116298
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