Advancing Transthyretin Amyloidosis Drug Development in an Evolving Treatment Landscape: Amyloidosis Forum Meeting Proceedings

Maurer, M. S., Soman, P., Hernandez, A., Garcia-Pavia, P., Signorovitch, J., Wei, L. J., Hanna, M., Ruberg, F. L., Kittleson, M., Kazi, D., Dorbala, S., Hsu, K., Lousada, I., Adigun, R., Dunnmon, P., Kelly, J., Gillmore, J., Masri, A., … Sanjurjo, V. (2024). Advancing Transthyretin Amyloidosis Drug Development in an Evolving Treatment Landscape: Amyloidosis Forum Meeting Proceedings. Advances in Therapy, 41(7), 2723–2742. https://doi.org/10.1007/s12325-024-02891-0
Authors:
Mathew S Maurer
Prem Soman
Adrian Hernandez
Pablo Garcia-Pavia
James Signorovitch
L J Wei
Mazen Hanna
Frederick L Ruberg
Michelle Kittleson
Dhruv Kazi
Sharmila Dorbala
Kristen Hsu
Isabelle Lousada
Rosalyn Adigun
Preston Dunnmon
Jeffery Kelly
Julian Gillmore
Affiliated Authors:
Mathew S Maurer
Author Keywords:
clinical trial design
drug development
rare diseases
transthyretin amyloidosis
Publication Type:
Article
Unique ID:
10.1007/s12325-024-02891-0
PMID:
Publication Date:
Data Source:
PubMed

Record Created: