Coratti, G., Civitello, M., Rohwer, A., Salmin, F., Glanzman, A. M., Montes, J., Pasternak, A., De Sanctis, R., Young, S. D., Duong, T., Mizzoni, I., Milev, E., Sframeli, M., Morando, S., Albamonte, E., D’Amico, A., Brolatti, N., Pane, M., Scoto, M., … Mercuri, E. (2024). Changes in abilities over the initial 12 months of nusinersen treatment for type II SMA. Neuromuscular Disorders, 41, 42–50. https://doi.org/10.1016/j.nmd.2024.05.003
Columbia Affiliation:
Subjects:
Oligonucleotides
(MeSH)
Publication Type:
Article
Unique ID:
10.1016/j.nmd.2024.05.003
PMID:
Journal:
Publication Date:
Data Source:
PubMed