Use of Ambroxol as Therapy for Gaucher Disease

Zhan, X., Zhang, H., Maegawa, G. H. B., Wang, Y., Gao, X., Wang, D., & Li, J. (2023). Use of Ambroxol as Therapy for Gaucher Disease. JAMA Network Open, 6(6), e2319364. https://doi.org/10.1001/jamanetworkopen.2023.19364

Authors:

Xia Zhan

Huiwen Zhang

Gustavo Maegawa

Yu Wang

Xiaolan Gao

Dengbin Wang

Jinning Li

Affiliated Authors:

Gustavo Maegawa

Columbia Affiliation:

Vagelos College of Physicians and Surgeons
- Department of Pediatrics

Subjects:

Gaucher Disease (MeSH)

Ambroxol (MeSH)

Lysosomal Storage Disorders in Human Health and Disease (OpenAlex Topic)

Mechanisms of Intracellular Membrane Trafficking (OpenAlex Topic)

Lysosomal Calcium Signaling in Physiology and Pathology (OpenAlex Topic)

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Publication Type:

Article

Unique ID:

10.1001/jamanetworkopen.2023.19364

PMID:

37342037

DOI:

10.1001/jamanetworkopen.2023.19364

Journal:

JAMA Network Open

Publication Date:

2023-06-21

Data Source:

OpenAlex

Source Link:

View OpenAlex Record

View PubMed Record

View Scopus Record

Record Created:

Monday, August 12, 2024 - 10:46