Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy: The MMPOWER-3 Randomized Clinical Trial

Karaa, A., Bertini, E., Carelli, V., Cohen, B. H., Enns, G. M., Falk, M. J., Goldstein, A., Gorman, G. S., Haas, R., Hirano, M., Klopstock, T., Koenig, M. K., Kornblum, C., Lamperti, C., Lehman, A., Longo, N., Molnar, M. J., Parikh, S., Phan, H., … Alessina, C. (2023). Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy. Neurology, 101(3). https://doi.org/10.1212/wnl.0000000000207402
Authors:
Amel Karaa
Enrico Bertini
Valerio Carelli
Bruce H Cohen
Gregory M Enns
Marni J Falk
Amy Goldstein
Gráinne Siobhan Gorman
Richard Haas
Michio Hirano
Thomas Klopstock
Mary Kay Koenig
Cornelia Kornblum
Costanza Lamperti
Anna Lehman
Nicola Longo
Maria Judit Molnar
Sumit Parikh
Han Phan
Robert D S Pitceathly
Russell Saneto
Fernando Scaglia
Serenella Servidei
Mark Tarnopolsky
Antonio Toscano
Johan L K Van Hove
John Vissing
Jerry Vockley
Jeffrey S Finman
David A Brown
James A Shiffer
Michelango Mancuso
Affiliated Authors:
Amel Karaa
Enrico Bertini
Valerio Carelli
Bruce H Cohen
Gregory M Enns
Marni J Falk
Amy Goldstein
Gráinne Siobhan Gorman
Richard Haas
Michio Hirano
Thomas Klopstock
Mary Kay Koenig
Cornelia Kornblum
Costanza Lamperti
Anna Lehman
Nicola Longo
Maria Judit Molnar
Sumit Parikh
Han Phan
Robert D S Pitceathly
Russell Saneto
Fernando Scaglia
Serenella Servidei
Mark Tarnopolsky
Antonio Toscano
Johan L K Van Hove
John Vissing
Jerry Vockley
Jeffrey S Finman
David A Brown
James A Shiffer
Michelango Mancuso
Subjects:
Publication Type:
Article
Unique ID:
10.1212/wnl.0000000000207402
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Journal:
Publication Date:
Data Source:
PubMed

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