Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5-year update of the NURTURE study

Crawford, T. O., Swoboda, K. J., De Vivo, D. C., Bertini, E., Hwu, W., Finkel, R. S., Kirschner, J., Kuntz, N. L., Nazario, A. N., Parsons, J. A., Pechmann, A., Ryan, M. M., Butterfield, R. J., Topaloglu, H., Ben‐Omran, T., Sansone, V. A., Jong, Y., Shu, F., … Zhu, C. (2023). Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of theNURTUREstudy. Muscle & Nerve, 68(2), 157–170. Portico. https://doi.org/10.1002/mus.27853
Authors:
Thomas O Crawford
Kathryn J Swoboda
Darryl C De Vivo
Enrico Bertini
Wuh-Liang Hwu
Richard S Finkel
Janbernd Kirschner
Nancy L Kuntz
Aledie Navas Nazario
Julie A Parsons
Astrid Pechmann
Monique M Ryan
Russell J Butterfield
Haluk Topaloglu
Tawfeg Ben-Omran
Valeria A Sansone
Yuh-Jyh Jong
Francy Shu
Cong Zhu
Stephanie Raynaud
Tiffany R Lago
Angela D Paradis
Richard Foster
Russell Chin
Zdenek Berger
Affiliated Authors:
Darryl C De Vivo
Columbia Affiliation:
Subjects:
Gene Therapy for Spinal Muscular Atrophy (OpenAlex Topic)
Etiology and Management of Abdominal Wall Defects (OpenAlex Topic)
RNA Methylation and Modification in Gene Expression (OpenAlex Topic)
Muscular Atrophy, Spinal (MeSH)
Spinal Muscular Atrophies of Childhood (MeSH)
Author Keywords:
motor function
nurture
nusinersen
safety
spinal muscular atrophy
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Publication Type:
Article
Unique ID:
10.1002/mus.27853
PMID:
37409780
DOI:
10.1002/mus.27853
Journal:
Muscle and Nerve
Publication Date:
Data Source:
PubMed
Source Link:
View PubMed Record
View Scopus Record
View OpenAlex Record

Record Created: