Crawford, T. O., Swoboda, K. J., De Vivo, D. C., Bertini, E., Hwu, W., Finkel, R. S., Kirschner, J., Kuntz, N. L., Nazario, A. N., Parsons, J. A., Pechmann, A., Ryan, M. M., Butterfield, R. J., Topaloglu, H., Ben‐Omran, T., Sansone, V. A., Jong, Y., Shu, F., … Zhu, C. (2023). Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of theNURTUREstudy. Muscle & Nerve, 68(2), 157–170. Portico. https://doi.org/10.1002/mus.27853
Subjects:
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Etiology and Management of Abdominal Wall Defects
(OpenAlex Topic)
RNA Methylation and Modification in Gene Expression
(OpenAlex Topic)
Muscular Atrophy, Spinal
(MeSH)
Publication Type:
Article
Unique ID:
10.1002/mus.27853
PMID:
DOI:
Journal:
Publication Date:
Data Source:
PubMed
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