Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study

Coratti, G., Bovis, F., Pera, M. C., Scoto, M., Montes, J., Pasternak, A., Mayhew, A., Muni‐Lofra, R., Duong, T., Rohwer, A., Dunaway Young, S., Civitello, M., Salmin, F., Mizzoni, I., Morando, S., Pane, M., Albamonte, E., D’Amico, A., … Brolatti, N. (2024). Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study. European Journal of Neurology, 31(8). Portico. https://doi.org/10.1111/ene.16309
Authors:
Giorgia Coratti
Francesca Bovis
Maria Carmela Pera
Mariacristina Scoto
Jacqueline Montes
Amy Pasternak
Anna Mayhew
Robert Muni‐Lofra
Tina Duong
Annemarie Rohwer
Sally Dunaway Young
Matthew Civitello
Francesca Salmin
Irene Mizzoni
Simone Morando
Marika Pane
Emilio Albamonte
Adèle D'Amico
Noemi Brolatti
Maria Sframeli
Chiara Marini‐Bettolo
Valeria Sansone
Claudio Bruno
Sonia Messina
Enrico Bertini
Giovanni Baranello
John Day
Basil T. Darras
Darryl C. De Vivo
Michio Hirano
Francesco Muntoni
Richard S. Finkel
Eugenio Mercuri
Affiliated Authors:
Jacqueline Montes
Darryl C. De Vivo
Michio Hirano
Author Keywords:
hammersmith functional motor scale expanded
minimal clinically important differences
minimal detectable change
spinal muscular atrophy
Publication Type:
Article
Unique ID:
10.1111/ene.16309
PMID:
Publication Date:
Data Source:
OpenAlex

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