Coratti, G., Bovis, F., Pera, M. C., Scoto, M., Montes, J., Pasternak, A., Mayhew, A., Muni‐Lofra, R., Duong, T., Rohwer, A., Dunaway Young, S., Civitello, M., Salmin, F., Mizzoni, I., Morando, S., Pane, M., Albamonte, E., D’Amico, A., … Brolatti, N. (2024). Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study. European Journal of Neurology, 31(8). Portico. https://doi.org/10.1111/ene.16309
Subjects:
Muscular Atrophy, Spinal
(MeSH)
Gene Therapy for Spinal Muscular Atrophy
(OpenAlex Topic)
Etiology and Management of Abdominal Wall Defects
(OpenAlex Topic)
Publication Type:
Article
Unique ID:
10.1111/ene.16309
PMID:
DOI:
Journal:
Publication Date:
Data Source:
OpenAlex